We have the largest, deepest,

ex-vivo gene therapy
data set in the world.


clinical and pre-clinical research
  • Pre-Clinical
  • Phase 1
  • Phase 2
  • Phase 3
  • PH 3 

    SCD (HGB-210)

  • PH 1/2 

    SCD (HGB-206)

bluebird bio, Inc. gene therapy for sickle cell disease is investigational and not FDA-approved. Safety and efficacy have not been established.