learned that when the
problem lies in your DNA,
there’s no simple way
to overcome

let's recode the building blocks

our focus

If it’s life-altering and difficult, we’re all in

We’re inspired by the people who live with a serious, life-altering disease but don’t let it stop them. The ones who keep pushing  reaching toward a day when they can live their lives fully. Because people in these situations are the ones who need help the most. So, we dig in to find new ways to recode the cells, reimagine the outcomes and rewrite the stories. It’s a quest that never gets old.
Two young boys playing with brightly colored stacking blocks on a living room floor

Learn about Cerebral Adrenoleukodystrophy

CALD is caused by accumulation of very-long chain fatty acids.
Family holding hands in a line at the beach

Learn about Transfusion-Dependent β-Thalassemia

TDT is characterized by reduced or absent functional β-globin.
Woman pausing on a path while walking her dog

Learn about Sickle Cell Disease

SCD is caused by production of abnormal hemoglobin.